Cincinnati Childrens

Our Vision Cincinnati Children’s Hospital Medical Center will be the leader in improving child health. Our Mission Cincinnati Children’s will improve child health and transform delivery of care through fully integrated, globally recognized research, education and innovation. For patients from our community, the nation and the world, the care we provide will achieve the best:

Sanguine Bio

Our mission is to develop innovative solutions that empower patients to participate in advancing research for conditions that matter most to them, regardless of their location or ability to travel. We work directly with patients and advocacy groups to accelerate research through convenience and transparency while guiding each patient every step of the way. Sign

Optum Frontier Therapies

It’s our mission to create access to therapies at the frontier of health care and to help all people, no matter how unique, access a better tomorrow.

Mirum Pharmaceuticals, Inc.

Mirum Pharmaceuticals, Inc. is a biopharmaceutical company dedicated to transforming the treatment of rare diseases. Mirum’s approved medication is LIVMARLI® (maralixibat) oral solution which is approved in the U.S. for the treatment of cholestatic pruritus in patients with Alagille syndrome one year of age and older. Please view the warnings and precautions available in the


Albireo is a global biopharmaceutical company focused on the development of novel bile acid modulators to treat rare pediatric and adult liver diseases. As leader in bile acid biology, we leverage our expertise in bile acid modulation with the goal of providing hope for families by delivering potentially transformative medicines. Our parent company, Albireo Pharma,


Our vision is to inspire hope in the PFIC community. Our mission is to improve the lives of patients and families worldwide affected by Progressive Familial Intrahepatic Cholestasis, PFIC. We value connection, education, and support to empower the community. We value providing relevant information for informed decision making, inclusivity, science and research, and collaboration. We

The Striped Spot – A Safe Online Community for Rare Kids

The Striped Spot is the only online community designed to be a safe space for rare disease kids. Parents must have an account before they can sign their child up and no adults are allowed in the professionally moderated kid-safe spaces. Join us for monthly support groups for patients and siblings or pop in to