Rare Rev Mag
Travere Therapeutics is a biopharmaceutical company whose mission is to identify, develop and deliver life-changing therapies to people living with rare disease.
Demo of an Exhibitor Booth
It’s our mission to create access to therapies at the frontier of health care and to help all people, no matter how unique, access a better tomorrow.
Mirum Pharmaceuticals, Inc. is a biopharmaceutical company dedicated to transforming the treatment of rare diseases. Mirum’s approved medication is LIVMARLI® (maralixibat) oral solution which is approved in the U.S. for the treatment of cholestatic pruritus in patients with Alagille syndrome one year of age and older. Please view the warnings and precautions available in the
Albireo is a global biopharmaceutical company focused on the development of novel bile acid modulators to treat rare pediatric and adult liver diseases. As leader in bile acid biology, we leverage our expertise in bile acid modulation with the goal of providing hope for families by delivering potentially transformative medicines. Our parent company, Albireo Pharma,
Our vision is to inspire hope in the PFIC community. Our mission is to improve the lives of patients and families worldwide affected by Progressive Familial Intrahepatic Cholestasis, PFIC. We value connection, education, and support to empower the community. We value providing relevant information for informed decision making, inclusivity, science and research, and collaboration. We